Natural history studies are specifically designed to study the natural progression or disease and to develop new outcome measures that can be utilized in Clinical Trials. These studies do not involve the intervention of a Food and Drug Administration (FDA) regulated drug or device.

Study Title Diagnosis Enrollment Status
Project 1 Natural History Study ALS, BMD, DMD, LGMD, MMD, FSH. SMA Type 2 & 3, ALS or Charcot Marie Tooth (CMT) Open
iFSHD Natural History Study Infantile Onset FSHD Open
DMD Tissue Bank Natural History Study DMD (Exon Skipping) Open
PRO-DMD Longitudinal Natural History Study DMD Open
DMD Longitudinal Natural History Study DMD Open
Ultrasound in ALS Natural History Study ALS  Open
BMD Natural History Study BMD  Open
Carpal Tunnel Syndrome Study Diagnosis of mild to moderate carpal tunnel syndrome or healthy volunteer Open